One-year results of the placebo-controlled ASCEND trial of olipudase alfa enzyme replacement therapy in adults with chronic acid sphingomyelinase deficiency


Wasserstein M., Arash-Kaps L., Barbato A., Gallagher R., Giugliani R., Guelbert N., ...More

MOLECULAR GENETICS AND METABOLISM, vol.132, 2021 (Peer-Reviewed Journal) identifier

  • Publication Type: Article / Abstract
  • Volume: 132
  • Publication Date: 2021
  • Journal Name: MOLECULAR GENETICS AND METABOLISM
  • Journal Indexes: Science Citation Index Expanded, Scopus, Academic Search Premier, BIOSIS, CAB Abstracts, Chemical Abstracts Core, EMBASE, MEDLINE, Veterinary Science Database